Familial Haploidentical Stem Cell Transplant in Children and Adolescents With High-Risk Sickle Cell Disease: A Phase 2 Clinical Trial. JAMA Pediatr 2020 Feb 01;174(2):195-197
Date
12/10/2019Pubmed ID
31816036Pubmed Central ID
PMC6902105DOI
10.1001/jamapediatrics.2019.4715Scopus ID
2-s2.0-85076336992 (requires institutional sign-in at Scopus site) 28 CitationsAbstract
This phase 2 clinical trial in patients with high-risk sickle cell disease assesses the feasibility, safety, and 1-year event-free survival after myeloimmunoablative conditioning and familial haploidentical stem cell transplant.
Author List
Cairo MS, Talano JA, Moore TB, Shi Q, Weinberg RS, Grossman B, Shenoy SAuthor
Julie-An M. Talano MD Professor in the Pediatrics department at Medical College of WisconsinMESH terms used to index this publication - Major topics in bold
AdolescentAnemia, Sickle Cell
Child
Child, Preschool
Female
Humans
Male
Prospective Studies
Risk Assessment
Stem Cell Transplantation
Young Adult









