Muscle-directed gene therapy corrects Pompe disease and uncovers species-specific GAA immunogenicity EMBO Molecular Medicine 11 January 2022;14(1)
Date
01/11/2022
DOI
10.15252/emmm.202113968Scopus ID
2-s2.0-85120325821 (requires institutional sign-in at Scopus site)
33 CitationsAuthor List
Eggers M, Vannoy CH, Huang J, Purushothaman P, Brassard J, Fonck C, Meng H, Prom MJ, Lawlor MW, Cunningham J, Sadhu C, Mavilio F
Author
Michael W. Lawlor MD, PhD Adjunct Professor in the Pathology department at Medical College of Wisconsin